World-first personalized gene-editing therapy saves infant from deadly disease in US. This marks the first instance of a completely customized CRISPR gene editing therapy in the world.
World-first personalized gene-editing therapy saves infant from deadly disease in US. This marks the first instance of a completely customized CRISPR gene editing therapy in the world.
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Drs Musunuru and Ahrens-Nicklas with KJ post infusion